A tractable, actionable path to CRISPR cures on demand is much closer than one might think. Ryan Cross of
@endpts.com reports in detail on this in a piece that covers work at the IGI and also Penn Medicine by Kiran Musunuru and colleagues.
We'll find a way or make one.
endpts.com/crispr-isnt-...
'Find a way, or make one': How two scientists hope to revitalize CRISPR's rare disease crisis
Fyodor Urnov and Kiran Musunuru advocate for streamlined CRISPR treatments for rare genetic diseases, partnering with Danaher and CHOP to develop custom therapies for HLH and metabolic disorders.
